Authors:
DJALILIAN AR
ARONOVICH EL
BRADSHAW JJ
CHO WF
OBRITSCH WF
CHAN CC
WHITLEY CB
KRACHMER JH
HOLLAND EJ
Citation: Ar. Djalilian et al., SUBCONJUNCTIVAL-LIMBAL INJECTION OF RETROVIRALLY TRANSDUCED FIBROBLASTS - A POSSIBLE APPROACH FOR GENE DELIVERY TO THE CORNEA, Investigative ophthalmology & visual science, 38(4), 1997, pp. 4411-4411
Authors:
WHITLEY CB
MCIVOR RS
PAN D
STRONCEK DF
ARONOVICH EL
BURGER SR
MCCULLOUGH J
Citation: Cb. Whitley et al., CLINICAL-TRIAL OF GENE-THERAPY FOR A MANNOSE-6-PHOSPHATE RECEPTOR-MEDIATED LYSOSOMAL STORAGE DISEASE, MUCOPOLYSACCHARIDOSIS TYPE-II (HUNTER-SYNDROME), American journal of human genetics, 61(4), 1997, pp. 2105-2105
Authors:
WHITLEY CB
MCIVOR RS
ARONOVICH EL
BERRY SA
BLAZAR BR
BURGER SR
KERSEY JH
KING RA
FARAS AJ
LATCHAW RE
MCCULLOUGH J
PAN D
RAMSAY NKC
STRONCEK DF
Citation: Cb. Whitley et al., RETROVIRAL-MEDIATED TRANSFER OF THE IDURONATE-2-SULFATASE GENE INTO LYMPHOCYTES FOR TREATMENT OF MILD HUNTER SYNDROME (MUCOPOLYSACCHARIDOSIS TYPE-II), Human gene therapy, 7(4), 1996, pp. 537-549
Authors:
BRAUN SE
PAN D
ARONOVICH EL
JONSSON JJ
MCIVOR RS
WHITLEY CB
Citation: Se. Braun et al., PRECLINICAL STUDIES OF LYMPHOCYTE GENE-THERAPY FOR MILD HUNTER SYNDROME (MUCOPOLYSACCHARIDOSIS TYPE-II), Human gene therapy, 7(3), 1996, pp. 283-290
Citation: El. Aronovich et al., MOLECULAR-GENETIC DEFECT UNDERLYING ALPHA-L-IDURONIDASE PSEUDODEFICIENCY, American journal of human genetics, 58(1), 1996, pp. 75-85
Authors:
ARONOVICH EL
PFISTER DR
HOLLAND EJ
PAN D
OBRITSCH W
SINCLAIR JM
BRADSHAW JJ
ANDERSON JA
KRACHMER JH
WHITLEY CB
Citation: El. Aronovich et al., PRECLINICAL STUDIES OF TOPICAL IN-VIVO GENE-THERAPY FOR SCHEIE KERATOPATHY ASSOCIATED WITH MUCOPOLYSACCHARIDOSIS TYPE-I, American journal of human genetics, 57(4), 1995, pp. 223-223
Citation: D. Pan et al., RETROVIRUS VECTOR STUDIES TOWARD HEMATOPOIETIC STEM-CELL GENE-THERAPYFOR MUCOPOLYSACCHARIDOSIS TYPE-I, American journal of human genetics, 57(4), 1995, pp. 1435-1435
Authors:
JONSSON JJ
ARONOVICH EL
BRAUN SE
WHITLEY CB
Citation: Jj. Jonsson et al., MOLECULAR DIAGNOSIS OF MUCOPOLYSACCHARIDOSIS TYPE-II (HUNTER SYNDROME) BY AUTOMATED SEQUENCING AND COMPUTER-ASSISTED INTERPRETATION - TOWARD MUTATION MAPPING OF THE IDURONATE-2-SULFATASE GENE, American journal of human genetics, 56(3), 1995, pp. 597-607
Authors:
WHITLEY CB
ANDERSON RA
ARONOVICH EL
CROTTY PL
ANYANEYEBOA K
RUSSO D
WARBURTON D
Citation: Cb. Whitley et al., CAVEAT TO GENOTYPE-PHENOTYPE CORRELATION IN MUCOPOLYSACCHARIDOSIS TYPE-II - DISCORDANT CLINICAL SEVERITY OF R468W-MUTATIONS AND R468Q-MUTATIONS OF THE IDURONATE-2-SULFATASE GENE, Human mutation, 2(3), 1993, pp. 235-237
Authors:
KRASNOPOLSKAYA KD
MIRENBURG TV
ARONOVICH EL
LEBEDEVA TV
ODINOKOVA ON
DEMINA NA
KOZLOVA VM
KUZNETSOV MI
Citation: Kd. Krasnopolskaya et al., DIAGNOSIS AND PREVENTION OF LYSOSOMAL STORAGE DISEASES IN RUSSIA, Journal of inherited metabolic disease, 16(6), 1993, pp. 994-1002
Authors:
BRAUN SE
ARONOVICH EL
ANDERSON RA
CROTTY PL
MCIVOR RS
WHITLEY CB
Citation: Se. Braun et al., METABOLIC CORRECTION AND CROSS-CORRECTION OF MUCOPOLYSACCHARIDOSIS TYPE-II (HUNTER SYNDROME) BY RETROVIRAL-MEDIATED GENE-TRANSFER AND EXPRESSION OF HUMAN IDURONATE-2-SULFATASE, Proceedings of the National Academy of Sciences of the United Statesof America, 90(24), 1993, pp. 11830-11834
Authors:
JONSSON JJ
BRAUN SE
PAN D
ARONOVICH EL
MCIVOR RS
WHITLEY CB
Citation: Jj. Jonsson et al., IN-VITRO CORRECTION OF IDURONATE-2-SULFATASE DEFICIENCY IN HUNTER SYNDROME (MUCOPOLYSACCHARIDOSIS TYPE-II) WITH 4 RETROVIRAL VECTORS, American journal of human genetics, 53(3), 1993, pp. 105-105
Authors:
BRAUN SE
JONSSON JJ
ARONOVICH EL
MCIVOR RS
WHITLEY CB
Citation: Se. Braun et al., A MODEL OF EX-VIVO LYMPHOCYTE GENE-THERAPY FOR HUNTER SYNDROME, MUCOPOLYSACCHARIDOSIS TYPE-II, American journal of human genetics, 53(3), 1993, pp. 409-409
Authors:
ARONOVICH EL
JONSSON JJ
BRAUN SE
WHITLEY CB
Citation: El. Aronovich et al., MOLECULAR-GENETIC DIAGNOSIS OF MUCOPOLYSACCHARIDOSIS TYPE-11 (HUNTER SYNDROME) USING AUTOMATED SEQUENCING AND COMPUTER-ASSISTED ANALYSIS, American journal of human genetics, 53(3), 1993, pp. 1120-1120