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Results: 1-15 |
Results: 15

Authors: FLOYD SS CLEMENS PR ONTELL MR KOCHANEK S DAY CS YANG J HAUSCHKA SD BALKIR L MORGAN J MORELAND MS FEERO GW EPPERLY M HUARD J
Citation: Ss. Floyd et al., EX-VIVO GENE-TRANSFER USING ADENOVIRUS-MEDIATED FULL-LENGTH DYSTROPHIN DELIVERY TO DYSTROPHIC MUSCLES, Gene therapy, 5(1), 1998, pp. 19-30

Authors: FEERO WG ROSENBLATT JD HUARD J WATKINS SC EPPERLY M CLEMENS PR KOCHANEK S GLORIOSO JC PARTRIDGE TA HOFFMAN EP
Citation: Wg. Feero et al., VIRAL GENE DELIVERY TO SKELETAL-MUSCLE - INSIGHTS ON MATURATION-DEPENDENT LOSS OF FIBER INFECTIVITY FOR ADENOVIRUS AND HERPES-SIMPLEX TYPE-1 VIRAL VECTORS, Human gene therapy, 8(4), 1997, pp. 371-380

Authors: CLEMENS PR CHEN HH MACK LM KELLY R ONTELL M KOCHANEK S
Citation: Pr. Clemens et al., PERSISTENT MUSCLE EXPRESSION FROM AN ADENOVIRAL VECTOR THAT LACKS ALLVIRAL GENES, Neurology, 48(3), 1997, pp. 11002-11002

Authors: CHEN HH MACK LM KELLY R ONTELL M KOCHANEK S CLEMENS PR
Citation: Hh. Chen et al., PERSISTENCE IN MUSCLE OF AN ADENOVIRAL VECTOR THAT LACKS ALL VIRAL GENES, Proceedings of the National Academy of Sciences of the United Statesof America, 94(5), 1997, pp. 1645-1650

Authors: HUARD J FLOYD SS VANDEUTEKOM JC ONTELL MR HAUSCHKA SD CLEMENS PR
Citation: J. Huard et al., MYOBLAST MEDIATED EX-VIVO GENE-TRANSFER OF FULL-LENGTH DYSTROPHIN TO MATURE DYSTROPHIC MUSCLE, American journal of human genetics, 61(4), 1997, pp. 2085-2085

Authors: CLEMENS PR KOCHANEK S SUNADA Y CHAN S CHEN HH CAMPBELL KP CASKEY CT
Citation: Pr. Clemens et al., IN-VIVO MUSCLE GENE-TRANSFER OF FULL-LENGTH DYSTROPHIN WITH AN ADENOVIRAL VECTOR THAT LACKS ALL VIRAL GENES, Gene therapy, 3(11), 1996, pp. 965-972

Authors: NORTH KN MILLER G IANNACCONE ST CLEMENS PR CHAD DA BELLA I SMITH TW BEGGS AH SPECHT LA
Citation: Kn. North et al., COGNITIVE DYSFUNCTION AS THE MAJOR PRESENTING FEATURE OF BECKERS MUSCULAR-DYSTROPHY, Neurology, 46(2), 1996, pp. 461-465

Authors: CLEMENS PR KRAUSE TL CHAN S KORB KE GRAHAM FL CASKEY CT
Citation: Pr. Clemens et al., RECOMBINANT TRUNCATED DYSTROPHIN MINIGENES - CONSTRUCTION, EXPRESSION, AND ADENOVIRAL DELIVERY, Human gene therapy, 6(11), 1995, pp. 1477-1485

Authors: CLEMENS PR KOCHANEK S CHAN S MITANI K CASKEY CT
Citation: Pr. Clemens et al., EXPRESSION OF FULL-LENGTH DYSTROPHIN AND BETA-GALACTOSIDASE IN-VITRO AND IN-VIVO - SOMATIC GENE-TRANSFER OF A NEW ADENOVIRAL VECTOR, American journal of human genetics, 57(4), 1995, pp. 221-221

Authors: KOCHANEK S CLEMENS PR MITANI K CHAN S CASKEY CT
Citation: S. Kochanek et al., A NEW ADENOVIRAL VECTOR FOR GENE-THERAPY - REPLACEMENT OF ALL VIRAL CODING SEQUENCES WITH 28 KB OF FOREIGN DNA, American journal of human genetics, 57(4), 1995, pp. 1414-1414

Authors: WEHNER M CLEMENS PR ENGEL AG KILIMANN MW
Citation: M. Wehner et al., HUMAN MUSCLE GLYCOGENOSIS DUE TO PHOSPHORYLASE-KINASE DEFICIENCY ASSOCIATED WITH A NONSENSE MUTATION IN THE MUSCLE ISOFORM OF THE ALPHA-SUBUNIT, Human molecular genetics, 3(11), 1994, pp. 1983-1987

Authors: CHAKRABORTY R ZHONG Y DEANDRADE M CLEMENS PR FENWICK RG CASKEY CT
Citation: R. Chakraborty et al., LINKAGE DISEQUILIBRIA AMONG (CA)(N) POLYMORPHISMS IN THE HUMAN DYSTROPHIN GENE AND THEIR IMPLICATIONS IN CARRIER DETECTION AND PRENATAL-DIAGNOSIS IN DUCHENNE AND BECKER MUSCULAR-DYSTROPHIES, Genomics, 21(3), 1994, pp. 567-570

Authors: CLEMENS PR KORB KE CASKEY CT
Citation: Pr. Clemens et al., TRUNCATION OF A MURINE DYSTROPHIN MINIGENE, Neurology, 44(4), 1994, pp. 10000229-10000229

Authors: CLEMENS PR CASKEY CT
Citation: Pr. Clemens et Ct. Caskey, GENE-THERAPY PROSPECTS FOR DUCHENNE MUSCULAR-DYSTROPHY, European neurology, 34(4), 1994, pp. 181-185

Authors: CLEMENS PR KORB KE MORSY MA NGO TT GRAHAM F CASKEY CT
Citation: Pr. Clemens et al., ADENOVIRAL VECTOR-MEDIATED GENE-TRANSFER OF BETA-GALACTOSIDASE INTO HUMAN MYOBLASTS AND MYOTUBES IN CULTURE, American journal of human genetics, 53(3), 1993, pp. 1144-1144
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