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Pauly, DF
Fraites, TJ
Toma, C
Bayes, HS
Huie, ML
Hirschhorn, R
Plotz, PH
Raben, N
Kessler, PD
Byrne, BJ
Citation: Df. Pauly et al., Intercellular transfer of the virally derived precursor form of acid alpha-glucosidase corrects the enzyme deficiency in inherited cardioskeletal myopathy Pompe disease, HUM GENE TH, 12(5), 2001, pp. 527-538
Authors:
Raben, N
Lu, N
Nagaraju, K
Rivera, Y
Lee, A
Yan, B
Byrne, B
Meikle, PJ
Umapathysivam, K
Hopwood, JJ
Plotz, PH
Citation: N. Raben et al., Conditional tissue-specific expression of the acid alpha-glucosidase (GAA)gene in the GAA knockout mice: implications for therapy, HUM MOL GEN, 10(19), 2001, pp. 2039-2047
Citation: B. Yan et al., Identification and characterization of a tissue-specific silencer element in the first intron of the human acid maltase gene, HUM GENET, 109(2), 2001, pp. 186-190
Authors:
Yan, B
Heus, J
Lu, N
Nichols, RC
Raben, N
Plotz, PH
Citation: B. Yan et al., Transcriptional regulation of the human acid alpha-glucosidase gene - Identification of a repressor element and its transcription factors Hes-1 and YY1, J BIOL CHEM, 276(3), 2001, pp. 1789-1793
Authors:
Nagaraju, K
Raben, N
Villalba, ML
Danning, C
Loeffler, LA
Lee, E
Tresser, N
Abati, A
Fetsch, P
Plotz, PH
Citation: K. Nagaraju et al., Costimulatory markers in muscle of patients with idiopathic inflammatory myopathies and in cultured muscle cells, CLIN IMMUNO, 92(2), 1999, pp. 161-169
Authors:
Adams, EM
Pucino, F
Yarboro, C
Hicks, JE
Thornton, B
McGarvey, C
Sonies, BC
Bartlett, ML
Villalba, ML
Fleisher, T
Plotz, PH
Citation: Em. Adams et al., A pilot study: Use of fludarabine for refractory dermatomyositis and polymyositis, and examination of endpoint measures, J RHEUMATOL, 26(2), 1999, pp. 352-360