Authors:
GWYNN B
LUEDERS K
SANDS MS
BIRKENMEIER EH
Citation: B. Gwynn et al., INTRACISTERNAL A-PARTICLE ELEMENT TRANSPOSITION INTO THE MURINE BETA-GLUCURONIDASE GENE CORRELATES WITH LOSS OF ENZYME-ACTIVITY - A NEW MODEL FOR BETA-GLUCURONIDASE DEFICIENCY IN THE C3H MOUSE, Molecular and cellular biology (Print), 18(11), 1998, pp. 6474-6481
Authors:
VOGLER C
SANDS MS
GALVIN N
LEVY B
THORPE C
BARKER J
SLY WS
Citation: C. Vogler et al., MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII - THE IMPACT OF THERAPIES ON THE CLINICAL COURSE AND PATHOLOGY IN A MURINE MODEL OF LYSOSOMAL STORAGEDISEASE, Journal of inherited metabolic disease, 21(5), 1998, pp. 575-586
Authors:
OCONNOR LH
ERWAY LC
VOGLER CA
SLY WS
NICHOLES A
GRUBB J
HOLMBERG SW
LEVY B
SANDS MS
Citation: Lh. Oconnor et al., ENZYME REPLACEMENT THERAPY FOR MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII LEADS TO IMPROVEMENTS IN BEHAVIOR AND AUDITORY FUNCTION, The Journal of clinical investigation, 101(7), 1998, pp. 1394-1400
Authors:
SANDS MS
VOGLER C
TORREY A
LEVY B
GWYNN B
GRUBB J
SLY WS
BIRKENMEIER EH
Citation: Ms. Sands et al., MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII - LONG-TERM THERAPEUTIC EFFECTSOF ENZYME REPLACEMENT AND ENZYME REPLACEMENT FOLLOWED BY BONE-MARROW TRANSPLANTATION, The Journal of clinical investigation, 99(7), 1997, pp. 1596-1605
Authors:
VOGLER C
SANDS MS
LEVY B
GALVIN N
BIRKENMEIER EH
SLY WS
Citation: C. Vogler et al., ENZYME REPLACEMENT WITH RECOMBINANT BETA-GLUCURONIDASE IN MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII - IMPACT OF THERAPY DURING THE FIRST 6 WEEKS OF LIFE ON SUBSEQUENT LYSOSOMAL STORAGE, GROWTH, AND SURVIVAL, Pediatric research, 39(6), 1996, pp. 1050-1054
Citation: Jh. Wolfe et al., HIGH-LEVEL EXPRESSION AND EXPORT OF BETA-GLUCURONIDASE FROM MURINE MUCOPOLYSACCHARIDOSIS-VII CELLS CORRECTED BY A DOUBLE-COPY RETROVIRUS VECTOR, Gene therapy, 2(1), 1995, pp. 70-78
Authors:
SANDS MS
VOGLER CA
GRUBB J
HIGGINS A
TORREY A
LEVY B
SLY WS
BIRKENMEIER EH
Citation: Ms. Sands et al., ENZYME REPLACEMENT WITH RECOMBINANT BETA-GLUCURONIDASE DRAMATICALLY REDUCES LYSOSOMAL STORAGE IN THE CNS OF MICE WITH MUCOPOLYSACCHARIDOSISTYPE-VII, Journal of cellular biochemistry, 1994, pp. 246-246
Authors:
BASTEDO L
SANDS MS
LAMBERT DT
PISA MA
BIRKENMEIER E
CHANG PL
Citation: L. Bastedo et al., BEHAVIORAL CONSEQUENCES OF BONE-MARROW TRANSPLANTATION IN THE TREATMENT OF MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII, The Journal of clinical investigation, 94(3), 1994, pp. 1180-1186
Authors:
SANDS MS
VOGLER C
KYLE JW
GRUBB JH
LEVY B
GALVIN N
SLY WS
BIRKENMEIER EH
Citation: Ms. Sands et al., ENZYME REPLACEMENT THERAPY FOR MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII, The Journal of clinical investigation, 93(6), 1994, pp. 2324-2331
Citation: Ms. Sands et Eh. Birkenmeier, A SINGLE-BASE-PAIR DELETION IN THE BETA-GLUCURONIDASE GENE ACCOUNTS FOR THE PHENOTYPE OF MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII, Proceedings of the National Academy of Sciences of the United Statesof America, 90(14), 1993, pp. 6567-6571
Authors:
SANDS MS
BARKER JE
VOGLER C
LEVY B
GWYNN B
GALVIN N
SLY WS
BIRKENMEIER E
Citation: Ms. Sands et al., TREATMENT OF MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII BY SYNGENEIC BONE-MARROW TRANSPLANTATION IN NEONATES, Laboratory investigation, 68(6), 1993, pp. 676-686
Authors:
KHIMANI L
SANDS MS
BIRKENMEIER EH
PISA MA
CHANG PL
Citation: L. Khimani et al., EFFECT OF BONE-MARROW TRANSPLANT OF THE BEHAVIORAL ABNORMALITIES OF AMURINE MODEL OF MUCOPOLYSACCHARIDOSIS TYPE-VII (SLY DISEASE), American journal of human genetics, 53(3), 1993, pp. 912-912