Authors:
FILLAT C
SIMONARO CM
YEYATI PL
ABKOWITZ JL
HASKINS ME
SCHUCHMAN EH
Citation: C. Fillat et al., ARYLSULFATASE-A ACTIVITIES AND GLYCOSAMINOGLYCAN LEVELS IN RETROVIRALLY TRANSDUCED MUCOPOLYSACCHARIDOSIS TYPE-VI CELLS - PROSPECTS FOR GENE-THERAPY, The Journal of clinical investigation, 98(2), 1996, pp. 497-502
Citation: Cm. Simonaro et Eh. Schuchman, N-ACETYLGALACTOSAMINE-4-SULFATASE - IDENTIFICATION OF 4 NEW MUTATIONSWITHIN THE CONSERVED SULFATASE REGION CAUSING MUCOPOLYSACCHARIDOSIS TYPE-VI, Biochimica et biophysica acta. Molecular basis of disease, 1272(3), 1995, pp. 129-132
Authors:
KUNIEDA T
SIMONARO CM
YOSHIDA M
IKADAI H
LEVAN G
DESNICK RJ
SCHUCHMAN EH
Citation: T. Kunieda et al., MUCOPOLYSACCHARIDOSIS TYPE-VI IN RATS - ISOLATION OF CDNAS ENCODING ARYLSULFATASE-B, CHROMOSOMAL LOCALIZATION OF THE GENE, AND IDENTIFICATION OF THE MUTATION, Genomics, 29(3), 1995, pp. 582-587
Authors:
SCHUCHMAN EH
YEYATI P
FILLAT C
SIMONARO CM
GATT S
HASKINS ME
DESNICK RJ
Citation: Eh. Schuchman et al., GENE-THERAPY FOR LYSOSOMAL STORAGE DISEASES - RETROVIRAL TRANSDUCTIONOF BONE-MARROW CELLS AND THE DEVELOPMENT OF DIRECT SELECTION METHODS, Journal of cellular biochemistry, 1995, pp. 433-433