Authors:
Aronovich, EL
Johnston, JM
Wang, P
Giger, U
Whitley, CB
Citation: El. Aronovich et al., Molecular basis of mucopolysaccharidosis type IIIB in emu (Dromaius novaehollandiae): An avian model of Sanfilippo syndrome type B, GENOMICS, 74(3), 2001, pp. 299-305
Authors:
Pan, D
Aronovich, E
McIvor, RS
Whitley, CB
Citation: D. Pan et al., Retroviral vector design studies toward hematopoietic stem cell gene therapy for mucopolysaccharidosis type I, GENE THER, 7(21), 2000, pp. 1875-1883
Authors:
Aronovich, EL
Carmichael, KP
Morizono, H
Koutlas, IG
Deanching, M
Hoganson, G
Fischer, A
Whitley, CB
Citation: El. Aronovich et al., Canine heparan sulfate sulfamidase and the molecular pathology underlying Sanfilippo syndrome type A in Dachshunds, GENOMICS, 68(1), 2000, pp. 80-84
Authors:
Pan, D
Shankar, R
Stroncek, DF
Whitley, CB
Citation: D. Pan et al., Combined ultrafiltration-transduction in a hollow-fiber bioreactor facilitates retrovirus-mediated gene transfer into peripheral blood lymphocytes from patients with mucopolysaccharidosis type II, HUM GENE TH, 10(17), 1999, pp. 2799-2810
Citation: Sd. Hartung et al., Enzymatic correction and cross-correction of mucopolysaccharidosis type I fibroblasts by adeno-associated virus-mediated transduction of the alpha-L-iduronidase gene, HUM GENE TH, 10(13), 1999, pp. 2163-2172
Authors:
Stroncek, DF
Hubel, A
Shankar, RA
Burger, SR
Pan, D
McCullough, J
Whitley, CB
Citation: Df. Stroncek et al., Retroviral transduction and expansion of peripheral blood lymphocytes for the treatment of mucopolysaccharidosis type II, Hunter's syndrome, TRANSFUSION, 39(4), 1999, pp. 343-350
Authors:
Hubel, A
Stroncek, D
Pan, D
Whitley, CB
McCullough, J
Citation: A. Hubel et al., Mobilization and transduction of peripheral blood progenitor cells in patients with mucopolysaccharidosis I, J HEMATOTH, 7(6), 1998, pp. 505-514