Ne. Breslow et N. Chatterjee, Design and analysis of two-phase studies with binary outcome applied to Wilms tumour prognosis, J ROY STA C, 48, 1999, pp. 457-468
Citations number
24
Categorie Soggetti
Mathematics
Journal title
JOURNAL OF THE ROYAL STATISTICAL SOCIETY SERIES C-APPLIED STATISTICS
Two-phase stratified sampling is used to select subjects for the collection
of additional data, e.g. validation data in measurement error problems. St
ratification jointly by outcome and covariates, with sampling fractions cho
sen to achieve approximately equal numbers per stratum at the second phase
of sampling, enhances efficiency compared with stratification based on the
outcome or covariates alone. Nonparametric maximum likelihood may result in
substantially more efficient estimates of logistic regression coefficients
than weighted or pseudolikelihood procedures. Software to implement all th
ree procedures is available. We demonstrate the practical importance of the
se design and analysis principles by an analysis of, and simulations based
on, data from the US National Wilms Tumor Study.