Authors:
RENDAHL KG
LEFF SE
OTTEN GR
SPRATT SK
BOHL D
VANROEY M
DONAHUE BA
COHEN LK
MANDEL RJ
DANOS O
SNYDER RO
Citation: Kg. Rendahl et al., REGULATION OF GENE-EXPRESSION IN-VIVO FOLLOWING TRANSDUCTION BY 2 SEPARATE RAAV VECTORS, Nature biotechnology, 16(8), 1998, pp. 757-761
Citation: K. Jooss et al., FUNCTION OF DENDRITIC CELLS IN THE INDUCTION OF IMMUNE-RESPONSES TO VIRAL VECTORS, Journal of leukocyte biology, 1998, pp. 8-8
Authors:
VINCENT N
DOUAR AM
DRITTANTI L
GLUZMAN R
SNYDER RO
DANOS O
Citation: N. Vincent et al., ADENOASSOCIATED VIRUS VECTORS FOR GENE-TRANSFER INTO NONDIVIDING CELLS IN-VIVO, Naunyn-Schmiedeberg's archives of pharmacology, 358(1), 1998, pp. 23-23
Citation: Jl. Battini et al., DEFINITION OF A 14-AMINO-ACID PEPTIDE ESSENTIAL FOR THE INTERACTION BETWEEN THE MURINE LEUKEMIA-VIRUS AMPHOTROPIC ENVELOPE GLYCOPROTEIN ANDITS RECEPTOR, Journal of virology, 72(1), 1998, pp. 428-435
Authors:
SNYDER RO
MIAO CH
PATIJN GA
SPRATT SK
DANOS O
NAGY D
GOWN AM
WINTHER B
MEUSE L
COHEN LK
THOMPSON AR
KAY MA
Citation: Ro. Snyder et al., PERSISTENT AND THERAPEUTIC CONCENTRATIONS OF HUMAN FACTOR-IX IN MICE AFTER HEPATIC GENE-TRANSFER OF RECOMBINANT AAV VECTORS, Nature genetics, 16(3), 1997, pp. 270-276
Authors:
SNYDER RO
SPRATT SK
LAGARDE C
BOHL D
KASPAR B
SLOAN B
COHEN LK
DANOS O
Citation: Ro. Snyder et al., EFFICIENT AND STABLE ADENOASSOCIATED VIRUS-MEDIATED TRANSDUCTION IN THE SKELETAL-MUSCLE OF ADULT IMMUNOCOMPETENT MICE, Human gene therapy, 8(16), 1997, pp. 1891-1900
Authors:
DAVIS JL
WITT RM
GROSS PR
HOKANSON CA
JUNGLES S
COHEN LK
DANOS O
SPRATT SK
Citation: Jl. Davis et al., RETROVIRAL PARTICLES PRODUCED FROM A STABLE HUMAN-DERIVED PACKAGING CELL-LINE TRANSDUCE TARGET-CELLS WITH VERY HIGH EFFICIENCIES, Human gene therapy, 8(12), 1997, pp. 1459-1467
Authors:
HOFLAND HEJ
NAGY D
LIU JJ
SPRATT K
LEE YL
DANOS O
SULLIVAN SM
Citation: Hej. Hofland et al., IN-VIVO GENE-TRANSFER BY INTRAVENOUS ADMINISTRATION OF STABLE CATIONIC LIPID DNA COMPLEX, Pharmaceutical research, 14(6), 1997, pp. 742-749
Authors:
NAFFAKH N
PINSET C
MONTARRAS D
LI ZL
PAULIN D
DANOS O
HEARD JM
Citation: N. Naffakh et al., LONG-TERM SECRETION OF THERAPEUTIC PROTEINS FROM GENETICALLY-MODIFIEDSKELETAL-MUSCLES, Human gene therapy, 7(1), 1996, pp. 11-21
Citation: C. Lavau et al., RETROVIRAL VECTORS FOR THE TRANSDUCTION OF THE PML-RAR-ALPHA FUSION PRODUCT OF ACUTE PROMYELOCYTIC LEUKEMIA, Experimental hematology, 24(4), 1996, pp. 544-551
Authors:
BATTINI JL
RODRIGUES P
MULLER R
DANOS O
HEARD JM
Citation: Jl. Battini et al., RECEPTOR-BINDING PROPERTIES OF A PURIFIED FRAGMENT OF THE 4070A AMPHOTROPIC MURINE LEUKEMIA-VIRUS ENVELOPE GLYCOPROTEIN, Journal of virology, 70(7), 1996, pp. 4387-4393
Authors:
LUTZKO C
KRUTH S
ABRAMSOGG A
LAU K
LU X
SHULL R
DANOS O
KOHN D
DUBE I
Citation: C. Lutzko et al., GENE-THERAPY FOR AN ENZYME DEFICIENCY STATE IS ABROGATED BY IMMUNE-RESPONSES TO GENE MODIFIED HEMATOPOIETIC STEM-CELLS, Blood, 88(10), 1996, pp. 1084-1084
Authors:
CHAMPSEIX C
MARECHAL V
KHAZAAL I
SCHWARTZ O
FOURNIER S
SCHLEGEL N
DRANOFF G
DANOS O
BLOT P
VILMER E
HEARD JM
PEAULT B
LEHN P
Citation: C. Champseix et al., A CELL-SURFACE MARKER GENE TRANSFERRED WITH A RETROVIRAL VECTOR INTO CD34(-BLOOD CELLS IS EXPRESSED BY THEIR T-CELL PROGENY IN THE SCID-HU THYMUS() CORD), Blood, 88(1), 1996, pp. 107-113
Authors:
HACEINBEY S
CAVAZZANACALVO M
LEDEIST F
DAUTRYVARSAT A
HIVROZ C
RIVIERE J
DANOS O
HEARD JM
SUGAMURA K
FISCHER A
BASILE GD
Citation: S. Haceinbey et al., GAMMA-C GENE-TRANSFER INTO SCID X1 PATIENTS B-CELL LINES RESTORES NORMAL HIGH-AFFINITY INTERLEUKIN-2 RECEPTOR EXPRESSION AND FUNCTION, Blood, 87(8), 1996, pp. 3108-3116
Authors:
MOULLIER P
BOHL D
CARDOSO J
HEARD JM
DANOS O
Citation: P. Moullier et al., LONG-TERM DELIVERY OF A LYSOSOMAL-ENZYME BY GENETICALLY-MODIFIED FIBROBLASTS IN DOGS, Nature medicine, 1(4), 1995, pp. 353-357
Authors:
SALVETTI A
MOULLIER P
CORNET V
BROOKS D
HOPWOOD JJ
DANOS O
HEARD JM
Citation: A. Salvetti et al., IN-VIVO DELIVERY OF HUMAN ALPHA-L-IDURONIDASE IN MICE IMPLANTED WITH NEO-ORGANS, Human gene therapy, 6(9), 1995, pp. 1153-1159
Citation: N. Enomaa et al., CORRECTION OF DEFICIENT ENZYME-ACTIVITY IN A LYSOSOMAL STORAGE DISEASE, ASPARTYLGLUCOSAMINURIA, BY ENZYME REPLACEMENT AND RETROVIRAL GENE-TRANSFER, Human gene therapy, 6(6), 1995, pp. 723-731
Authors:
CARREAU M
QUILLIET X
EVENO E
SALVETTI A
DANOS O
HEARD JM
MEZZINA M
SARASIN A
Citation: M. Carreau et al., FUNCTIONAL RETROVIRAL VECTOR FOR GENE-THERAPY OF XERODERMA-PIGMENTOSUM GROUP-D PATIENTS, Human gene therapy, 6(10), 1995, pp. 1307-1315
Authors:
VALERE T
BOHL D
KLATZMANN D
DANOS O
SONIGO P
HEARD JM
Citation: T. Valere et al., CONTINUOUS SECRETION OF HUMAN SOLUBLE CD4 IN MICE TRANSPLANTED WITH GENETICALLY-MODIFIED CELLS, Gene therapy, 2(3), 1995, pp. 197-202
Authors:
NAFFAKH N
MOULLIER P
SALVETTI A
BOHL D
DANOS O
HEARD JM
Citation: N. Naffakh et al., DELIVERY OF THERAPEUTIC PROTEINS FROM GENETICALLY-MODIFIED CELLS, Restorative neurology and neuroscience, 8(1-2), 1995, pp. 67-69
Authors:
DWARKI VJ
BELLONI P
NIJJAR T
COUTO L
CHIN R
SHANKARA S
SPRATT K
COHEN L
DANOS O
MULLIGAN R
Citation: Vj. Dwarki et al., GENE-THERAPY FOR HEMOPHILA-A-AND-B - RETROVIRAL AND ADENOVIRAL MEDIATED GENE-TRANSFER, Journal of cellular biochemistry, 1995, pp. 375-375
Authors:
BRAUKER J
DWARKI V
CARRBRENDEL V
NIJJAR T
VERGOTH C
CHEN R
COHEN L
DANOS O
MULLIGAN R
JOHNSON RC
Citation: J. Brauker et al., EXPRESSION OF HUMAN FACTOR-IX IN RATS AND MICE FROM CELLS IMPLANTED WITHIN AN IMMUNOISOLATION DEVICE, Journal of cellular biochemistry, 1995, pp. 375-375
Citation: Jl. Davis et al., A PACKAGING CELL-LINE TO GENERATE HIGH-TITER RECOMBINANT RETROVIRUS OF VARYING PSEUDOTYPES, Journal of cellular biochemistry, 1995, pp. 404-404
Authors:
NAFFAKH N
HENRI A
VILLEVAL JL
ROUYERFESSARD P
MOULLIER P
BLUMENFELD N
DANOS O
VAINCHENKER W
HEARD JM
BEUZARD Y
Citation: N. Naffakh et al., SUSTAINED DELIVERY OF ERYTHROPOIETIN IN MICE BY GENETICALLY-MODIFIED SKIN FIBROBLASTS, Proceedings of the National Academy of Sciences of the United Statesof America, 92(8), 1995, pp. 3194-3198