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Authors: DUNBAR CE KOHN DB SCHIFFMANN R BARTON NW NOLTA JA ESPLIN JA PENSIERO M LONG ZF LOCKEY C EMMONS RVB CSIK S LEITMAN S KREBS CB CARTER C BRADY RO KARLSSON S
Citation: Ce. Dunbar et al., RETROVIRAL TRANSFER OF THE GLUCOCEREBROSIDASE GENE INTO CD34(-DISEASE- IN-VIVO DETECTION OF TRANSDUCED CELLS WITHOUT MYELOABLATION() CELLSFROM PATIENTS WITH GAUCHER), Human gene therapy, 9(17), 1998, pp. 2629-2640

Authors: ARGOFF CE BARTON NW BRADY RO ZIESSMAN HA
Citation: Ce. Argoff et al., GASTROINTESTINAL SYMPTOMS AND DELAYED GASTRIC-EMPTYING IN FABRYS-DISEASE - RESPONSE TO METOCLOPRAMIDE, Nuclear medicine communications, 19(9), 1998, pp. 887-891

Authors: CRUTCHFIELD KE PATRONAS NJ DAMBROSIA JM FREI KP BANERJEE TK BARTON NW SCHIFFMANN R
Citation: Ke. Crutchfield et al., QUANTITATIVE-ANALYSIS OF CEREBRAL VASCULOPATHY IN PATIENTS WITH FABRY-DISEASE, Neurology, 50(6), 1998, pp. 1746-1749

Authors: SCHIFFMANN R DWYER NK LUBENSKY IA TSOKOS M SUTLIFF VE LATIMER JS FREI KP BRADY RO BARTON NW BLANCHETTEMACKIE EJ GOLDIN E
Citation: R. Schiffmann et al., CONSTITUTIVE ACHLORHYDRIA IN MUCOLIPIDOSIS TYPE-IV, Proceedings of the National Academy of Sciences of the United Statesof America, 95(3), 1998, pp. 1207-1212

Authors: TEDESCHI G BONAVITA S BARTON NW BERTOLINO A FRANK JA PATRONAS NJ ALGER JR SCHIFFMANN R
Citation: G. Tedeschi et al., PROTON MAGNETIC-RESONANCE SPECTROSCOPIC IMAGING IN THE CLINICAL-EVALUATION OF PATIENTS WITH NIEMANN-PICK TYPE-C DISEASE, Journal of Neurology, Neurosurgery and Psychiatry, 65(1), 1998, pp. 72-79

Authors: SCHIFFMANN R HEYES MP AERTS JM DAMBROSIA JM PATTERSON MC DEGRABA T PARKER CC ZIRZOW GC OLIVER K TEDESCHI G BRADY RO BARTON NW NAGINENI C KANESKI CR MURRAY GJ HIGGINS JJ TOURNAY A BANERJEE TK KREPS C SCOTT LJC MCKEE MA CRUTCHFIELD K FREI K
Citation: R. Schiffmann et al., PROSPECTIVE-STUDY OF NEUROLOGICAL RESPONSES TO TREATMENT WITH MACROPHAGE-TARGETED GLUCOCEREBROSIDASE IN PATIENTS WITH TYPE-3 GAUCHERS-DISEASE, Annals of neurology, 42(4), 1997, pp. 613-621

Authors: SCHIFFMANN R TEDESCHI G KINKEL RP TRAPP BD FRANK JA KANESKI CR BRADY RO BARTON NW NELSON L YANOVSKI JA
Citation: R. Schiffmann et al., LEUKODYSTROPHY IN PATIENTS WITH OVARIAN DYSGENESIS, Annals of neurology, 41(5), 1997, pp. 654-661

Authors: HILL SC BAKER AR BARTON NW WEXLER LH SCOTT LJC
Citation: Sc. Hill et al., SCIATIC-NERVE - PARADOXIC HYPERTROPHY AFTER AMPUTATION IN YOUNG-PATIENTS, Radiology, 205(2), 1997, pp. 559-562

Authors: BRADY RO MURRAY GJ OLIVER KL LEITMAN SF SNELLER MC FLEISHER TA BARTON NW
Citation: Ro. Brady et al., MANAGEMENT OF NEUTRALIZING ANTIBODY TO CEREDASE IN A PATIENT WITH TYPE-3 GAUCHER-DISEASE, Pediatrics, 100(6), 1997, pp. 111-114

Authors: CRUTCHFIELD KE PETRONAS NJ BANERJEE TK BARTON NW DAMBROSIA M FREI KP TOUNAY AE LELAND JCS BRADY R SCHIFFMAN R
Citation: Ke. Crutchfield et al., QUANTIFICATION OF FABRY-DISEASE PROGRESSION UTILIZING CEREBRAL MRI, Neurology, 48(3), 1997, pp. 56002-56002

Authors: DUNBAR CE KOHN DB SCHIFFMAN R BARTON NW NOLTA J WELLS S ESPLIN J PENSIERO M EMMONS RVB LEITMAN S KREPS CB CARTER C KIMBALL J YOUNG NS BRADY RO KARLSSON S
Citation: Ce. Dunbar et al., RETROVIRAL GENE-TRANSFER OF THE GLUCOCEREBROSIDASE GENE INTO PB OR BMCD34-DISEASE - RESULTS FROM A CLINICAL-TRIAL( CELLS FROM PATIENTS WITH GAUCHER), Blood, 90(10), 1997, pp. 1044-1044

Authors: GRABOWSKI GA SAAL HM WENSTRUP RJ BARTON NW
Citation: Ga. Grabowski et al., GAUCHER DISEASE - A PROTOTYPE FOR MOLECULAR MEDICINE, Critical reviews in oncology/hematology, 23(1), 1996, pp. 25-55

Authors: BARTON NW HOUSTON DC
Citation: Nw. Barton et Dc. Houston, FACTORS INFLUENCING THE SIZE OF SOME INTERNAL ORGANS IN RAPTORS, The Journal of raptor research, 30(4), 1996, pp. 219-223

Authors: HILL SC DAMASKA BM TSOKOS M KREPS C BRADY RO BARTON NW
Citation: Sc. Hill et al., RADIOGRAPHIC FINDINGS IN TYPE 3B GAUCHER DISEASE, Pediatric radiology, 26(12), 1996, pp. 852-860

Authors: MCCABE ERB FINE BA GOLBUS MS GREENHOUSE JB MCGRATH GL NEW M OBRIEN WE ROWLEY PT SLY WS SPENCE MA STOCKMAN JA WHYTE M WILSON W WOLF B AERTS JMFG BARRANGER JA BARTON NW BEUTLER E BRADY RO COX TM EKSTEIN J ENG CM ERIKSON A FINDLING DM GARBER AM GINNS EI GRABOWSKI GA HILL SC HOLLACK CEM KABACK MM LEE RE MANKIN HJ MISTRY PK MOSCICKI RA MURRAY GJ NATOWICZ M PASTORES GM MIRANDA MCS SIDRANSKY E WARE JE WILLEMSEN R ZAIZOV R ZIMRAN A BEITINS IZ BERMAN RE ELLIOTT JM FERGUSON JH HALL WH MCKEON C NITKIN RM SCHLESINGER SL SHERIDAN PH WEEKS M COWDRY RW ALEXANDER DF GORDEN P HALL ZW VAITUKAITIS JL COLLINS FS GROFT S
Citation: Erb. Mccabe et al., GAUCHER DISEASE - CURRENT ISSUES IN DIAGNOSIS AND TREATMENT, JAMA, the journal of the American Medical Association, 275(7), 1996, pp. 548-553

Authors: SCHIFFMANN R PARKER CC SCOTT LJC DEGRABA T BRADY RO BARTON NW
Citation: R. Schiffmann et al., A PROSPECTIVE-STUDY OF ENZYME REPLACEMENT THERAPY IN TYPE-3 GAUCHER DISEASE, Neurology, 46(2), 1996, pp. 1107-1107

Authors: BRADY RO BARTON NW
Citation: Ro. Brady et Nw. Barton, ENZYME REPLACEMENT AND GENE-THERAPY FOR GAUCHERS-DISEASE, Lipids, 31, 1996, pp. 137-139

Authors: MILLER SPF ZIRZOW GC DOPPELT SH BRADY RO BARTON NW
Citation: Spf. Miller et al., ANALYSIS OF THE LIPIDS OF NORMAL AND GAUCHER BONE-MARROW, The Journal of laboratory and clinical medicine, 127(4), 1996, pp. 353-358

Authors: OHSHIMA T MURRAY GJ NAGLE JW QUIRK JM KRAUS MH BARTON NW BRADY RO KULKARNI AB
Citation: T. Ohshima et al., STRUCTURAL ORGANIZATION AND EXPRESSION OF THE MOUSE GENE ENCODING ALPHA-GALACTOSIDASE-A, Gene, 166(2), 1995, pp. 277-280

Authors: SCHIFFMANN R YANOVSKI JA TEDESCHI G KINKEL RP BRADY RO DICHIRO G BARTON NW
Citation: R. Schiffmann et al., OVARIOLEUKODYSTROPHY - A NEW WHITE-MATTER SYNDROME, Annals of neurology, 38(3), 1995, pp. 547-547

Authors: ROSENTHAL DI DOPPELT SH MANKIN HJ DAMBROSIA JM XAVIER RJ MCKUSICK KA ROSEN BR BAKER J NIKLASON LT HILL SC MILLER SPF BRADY RO BARTON NW
Citation: Di. Rosenthal et al., ENZYME REPLACEMENT THERAPY FOR GAUCHER DISEASE - SKELETAL RESPONSES TO MACROPHAGE-TARGETED GLUCOCEREBROSIDASE, Pediatrics, 96(4), 1995, pp. 629-637

Authors: TEDESCHI G SCHIFFMANN R BARTON NW SHIH HHL GOSPE SM BRADY RO ALGER JR DICHIRO G
Citation: G. Tedeschi et al., PROTON MAGNETIC-RESONANCE SPECTROSCOPIC IMAGING IN CHILDHOOD ATAXIA WITH DIFFUSE CENTRAL-NERVOUS-SYSTEM HYPOMYELINATION, Neurology, 45(8), 1995, pp. 1526-1532

Authors: RUSSELL JW LUCIANO CA BANERJEE TK QUIRK JM SCOTT LJC BRADY RO BARTON NW
Citation: Jw. Russell et al., CLINICAL AND ELECTROPHYSIOLOGIC STUDIES OF MYELINATED AND UNMYELINATED FIBER FUNCTIONS IN FABRY DISEASE, Neurology, 45(4), 1995, pp. 227-228

Authors: ZIMRAN A ELSTEIN D SCHIFFMANN R ABRAHAMOV A GOLDBERG M BARMAOR JA BRADY RO GUZZETTA PC BARTON NW
Citation: A. Zimran et al., OUTCOME OF PARTIAL SPLENECTOMY FOR TYPE-I GAUCHER DISEASE, The Journal of pediatrics, 126(4), 1995, pp. 596-597

Authors: GRABOWSKI GA BARTON NW PASTORES G DAMBROSIA JM BANERJEE TK MCKEE MA PARKER C SCHIFFMANN R HILL SC BRADY RO
Citation: Ga. Grabowski et al., ENZYME THERAPY IN TYPE-1 GAUCHER DISEASE - COMPARATIVE EFFICACY OF MANNOSE-TERMINATED GLUCOCEREBROSIDASE FROM NATURAL AND RECOMBINANT SOURCES, Annals of internal medicine, 122(1), 1995, pp. 33-39
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